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Trial Match

Clinical trials test new treatments — sometimes the newest options available for a disease. Find trials that are recruiting now, near you. Open one to see its eligibility rules as simple questions to go through with your doctor.

Know your stage or your test results (such as EGFR, HER2 or BRCA)? Match trials to your own profile - nothing you type is saved.

🎯 Match trials to me

11 recruiting trials

for Orphan Diseases

Education & Care in RARE: Efficacy of Targeted Psychoeducational Intervention Among Pediatric Rare Disease Patients NCT06729554NA7 sites📍 Graz📍 Innsbruck📍 Linz Medical University of Vienna · Tests: Education & Care in RARE European Management Platform for Childhood Interstitial Lung Diseases - chILD-EU Register and Biobank NCT02852928n/a3 sites📍 Hanover📍 Ankara📍 Edinburgh Matthias Griese Reversing External-beam Radiotherapy-associated Fibrosis Syndrome: an Interventional Bayesian Adaptive Randomized-controlled Orphan Drug Platform Trial for Orodental Sequelae (Reverse-fibrose) NCT06912763Phase 21 site📍 Houston M.D. Anderson Cancer Center · Tests: Pravastatin (drug), Pentoxifylline, ketoprofen, Pirfenidoneone, Standard of Care (SOC) A First-in-Human Clinical Trial to Evaluate the Safety, Tolerability, and Efficacy of a Novel CRISPR RNA-editing Therapy in Patients with Mecp2 Duplication Syndrome, a Rare Orphan Disease (HERO) NCT06615206NA1 site📍 Beijing HuidaGene Therapeutics Co., Ltd. · Tests: HG204 Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford NCT01793168n/a2 sites📍 Sioux Falls📍 Sydney Sanford Health Gene Discovery Core, The Manton Center NCT02743845n/a1 site📍 Boston Boston Children's Hospital Automatic Phenotyping of Patients on 2D Photography NCT06219421n/a1 site📍 Paris Imagine Institute · Tests: Clinical data reuse Vascular Disease Discovery Protocol NCT03538639n/a1 site📍 Bethesda National Heart, Lung, and Blood Institute (NHLBI) RAPA-501 Therapy for ALS NCT04220190Phase 2, Phase 31 site📍 Boston Rapa Therapeutics LLC · Tests: RAPA-501 Autologous T stem cells Safety, Tolerability, and Preliminary Effectiveness of CTH120 in Fragile X Syndrome NCT07654114Phase 22 sites📍 Barcelona📍 Sabadell Connecta Therapeutics, S.L. · Tests: CTH120, CTH120 placebo hard capsules Orphan Europe Carbaglu® Surveillance Protocol NCT03409003n/a3 sites📍 Washington D.C.📍 Boston📍 New York Nicholas Ah Mew
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