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โ† Trials
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Long Term Trajectories of SMA Patients Receiving or Not Disease-modifying Treatments

Recruitingn/aAges any - anyAllFondazione Policlinico Universitario Agostino Gemโ€ฆ
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In plain words

What the trial is, and whether it could suit you

This is an observational multicenter retrospective and prospective study on natural history of SMA also considering the 'new natural history' secondary to the availability of commercially available therapies. All the patients enrolled to date in the Italian registry, if not part of clinical trials, will be included in the present study.

Sign in to get the eligibility rules as simple questions to take to your doctor.

๐Ÿ“‹ Eligibility rules (as published)
Inclusion Criteria: all patients with mutationsin the SMAN1 gene Exclusion Criteria: unable to proviude consent
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What it tests

  • Not listed
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Where

5 sites
Istituto Gaslini
Genova, Italy
Nemo Sud
Messina, Italy
Centro Clinico nemo
Milan, Italy
Ospedale Bambino gesu
Rome, Italy
Policlinico gemelli
Rome, Italy
๐Ÿค Taking part is your choice, and you can leave at any time. Only the trial team can confirm you are eligible โ€” always decide together with your own doctor.
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