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โ† Trials
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VIrtual STudy in Achondroplasia for the US (VISTA)

Recruitingn/aAges 0 Months - 18 YearsAllBioMarin Pharmaceutical
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In plain words

What the trial is, and whether it could suit you

This is an observational study of individuals with achondroplasia in the United States. The primary study population consists of pediatric individuals treated and untreated with VOXZOGOโ„ข. Study enrollment started in February 2023. The projected total duration of the study is approximately 5 years at minimum from start of study recruitment in February 2023, with the duration of individual prospective follow-up differing depending on the time of enrollment. The study duration may be extended based on decisions by the study sponsor. Data will be collected in two formats for the primary pediatric study population: 1. Participant-mediated access to electronic health records(including medical imaging, when available) which will enable retrospective and prospective collection of secondary data reflecting real-life treatment use and clinical care. . 2. Primary data collection of Clinical Outco

Sign in to get the eligibility rules as simple questions to take to your doctor.

๐Ÿ“‹ Eligibility rules (as published)
Inclusion Criteria: * Physician diagnosis of achondroplasia * Age at time of enrollment: Primary Pediatric Cohort: โ‰ค13 years old Secondary Adolescent and Adult Cohort: โ‰ฅ14 years old * Receiving medical care in the United States * Complete PicnicHealth's onboarding process, including signing informed consent and authorization for medical record retrieval Exclusion Criteria: * Lack of any medical records
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What it tests

  • Not listed
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Where

8 sites
UCSF
Oakland, United States
PicnicHealth
San Francisco, United States
Johns Hopkins University (JHU)
Baltimore, United States
Piedmont Health
Statesville, United States
University of Cincinnati
Cincinnati, United States
Sanford Health
Sioux Falls, United States
Baylor College of Medicine
Houston, United States
University of Wisconsin
Madison, United States
๐Ÿค Taking part is your choice, and you can leave at any time. Only the trial team can confirm you are eligible โ€” always decide together with your own doctor.
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