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A Study of Participants with Β-Thalassemia Treated with Betibeglogene Autotemcel

Recruitingn/aAges any - anyAllGenetix Biotherapeutics Inc.
NCT06271512 on ClinicalTrials.gov ↗
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In plain words

What the trial is, and whether it could suit you

The main aim of this study is to collect real-world longitudinal data on participants with β-thalassemia treated with betibeglogene autotemcel (beti-cel) in the post marketing setting. To assess the long-term safety, including the risk of newly diagnosed malignancies, after treatment with beti-cel and evaluate the long-term effectiveness of treatment with beti-cel.

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📋 Eligibility rules (as published)
Inclusion Criteria: * Participant must be treated with beti-cel in the post marketing setting at a center in the US that participates in the Registry. * Participant must sign an informed consent and/or assent prior to enrollment as required under applicable laws and regulations. * Participant must have signed an informed consent and/or assent permitting data to be shared with Center for International Blood and Marrow Transplant Research (CIBMTR). * Participant must be followed by a hematologist based in the US. Exclusion Criteria: \- There are no exclusion criteria for Registry participation.
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What it tests

  • No Intervention
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Where

6 sites
UCSF Benioff Children's Hospitals
Oakland, United States
Stanford University
Palo Alto, United States
University of Minnesota
Minneapolis, United States
Cohen Children's Medical Center
New Hyde Park, United States
Children's Hospital of Philadelphia
Philadelphia, United States
Texas Children's Hospital
Houston, United States
🤝 Taking part is your choice, and you can leave at any time. Only the trial team can confirm you are eligible — always decide together with your own doctor.
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