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Home Reported Outcomes in PNH

Recruitingn/aAges 18 Years - 99 YearsAllNovartis Pharmaceuticals
NCT06411626 on ClinicalTrials.gov ↗
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In plain words

What the trial is, and whether it could suit you

The study aims to longitudinally capture the full spectrum of symptoms, treatment utilization, and overall Health-Related Quality of Life (HRQoL) experienced by PNH patients. By primarily utilizing home reported outcomes (HRO) data on symptom burden and treatment usage, supplemented with patient-reported outcome (PRO) measures, the study seeks to establish a new real-world data (RWD) source to understand symptom variability and HRQoL among PNH patients, including those receiving orally administered iptacopan.

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📋 Eligibility rules (as published)
Inclusion Criteria: Study participants eligible for inclusion in this study must meet all of the following criteria: * Aged 18 or older * US-based with a proficient understanding of and ability to read the English language * Any patient with a diagnosis of PNH, regardless of symptom or treatment history Exclusion Criteria: Study participants who do not fit all inclusion criteria listed above are unable to participate in this study. Outside of required inclusion criteria, there are no other exclusion criteria in order to meet the exploratory nature of the primary endpoint.
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What it tests

  • PNH-relevant therapies
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Where

1 site
Novartis Investigative Site
East Hanover, United States
🤝 Taking part is your choice, and you can leave at any time. Only the trial team can confirm you are eligible — always decide together with your own doctor.
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