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A Study to Investigate the Efficacy and Safety of Fitusiran Prophylaxis in Male Participants Aged 1 to Less Than 12 Years With Hemophilia A or B

RecruitingPhase 3Ages 1 Year - 11 YearsMaleSanofi
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In plain words

What the trial is, and whether it could suit you

This is a parallel, Phase 3, two-arm, open-label study to evaluate the efficacy and safety of treatment with fitusiran prophylaxis administered to male pediatric participants (aged 1 to \<12 years) who have severe hemophilia A or B, with or without inhibitory antibodies to FVIII or FIX. Number of participants: Approximately 85 participants will be enrolled into the study: * Approximately 60 fitusiran-naïve participants with severe hemophilia A or B, with or without inhibitors (fitusiran-naïve arm), and * Approximately 25 participants with severe hemophilia A or B with inhibitors rolling over from the EFC15467\* dose confirmation study (roll-over arm). * Fitusiran has been investigated in the pediatric population in study EFC15467, which enrolled male participants aged 1 to \<12 years with hemophilia A or B with inhibitors to examine the safety and tolerability of fitusiran in the p

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📋 Eligibility rules (as published)
Inclusion Criteria: Participants not previously exposed to fitusiran are eligible to be included in the study only if all of the following criteria apply: * Participant must be 1 to \<12 years of age at the time of enrollment. * Participants must have severe hemophilia A or B (FVIII \<1% or FIX ≤2%) as evidenced by a central laboratory measurement at screening or documented medical record evidence. * Participants must meet inhibitor or non-inhibitor status as defined below: Inhibitor: Requiring use of BPA for prophylaxis or BPA as on-demand therapy for any bleeding episodes for at least the last 3 months prior to screening, and meet one of the following Nijmegen-modified Bethesda assay results criteria: * Inhibitor titer of ≥0.6 BU/mL at screening, OR * Inhibitor titer of \<0.6 BU/mL at screening with medical record evidence of 2 consecutive titers ≥0.6 BU/mL, OR * Inhibitor titer of \<0.6 BU/mL at screening with medical record evidence of 1 inhibitor titer ≥0.6 BU/mL and a history of anamnestic response, or severe allergic reaction (eg, anaphylaxis) or nephrotic syndrome Non-inhibitor: Requiring use of clotting factor concentrates (CFCs) for prophylaxis or CFCs as on-demand therapy for any bleeding episodes for at least the last 3 months prior to screening, and meet each of the following criterion: * Nijmegen-modified Bethesda assay inhibitor titer of \<0.6 BU/mL at screening, AND * No use of BPA to treat bleeding episodes for at least the last 3 months prior to screening * Participants must have adequate peripheral venous access, as determined by the Investigator, to allow the blood draws required by the study protocol. * Male: There are no contraceptive requirements for this study except where required by local regulations. * Capable of giving signed informed consent/assent. A signed written informed consent must be obtained from parent(s)/legal guardian (hereafter referred to as the "parent"), as well as a written or oral assent obtained from participant, per local and national requirements. Exclusion Criteria: Participants not previously exposed to fitusiran are excluded from the study if any of the following criteria apply: * Known co-existing bleeding disorders other than hemophilia A or B. * Presence of clinically significant liver disease. * History of antiphospholipid antibody syndrome. * History of arterial or venous thromboembolism, unrelated to an indwelling venous access * Any condition (eg, medical concern), which in the opinion of the Investigator, would make the participant unsuitable for dosing or which could interfere with the study compliance, the participant's safety and/or the participant's participation in the completion of the treatment period of the study. * History of multiple drug allergies or history of allergic reaction to an oligonucleotide or GalNAc. * Subjects with a central or peripheral indwelling catheter, with a history of venous access complications (such as infections, thrombosis) leading to hospitalization and/or systemic anticoagulation therapy in the last 12 months. * At screening, anticipated need of surgery during the study or planned surgery scheduled to occur during the study. * Completion of a surgical procedure within 14 days prior to screening, or currently receiving additional BPA infusion for postoperative hemostasis. * History of intolerance to SC injection(s). * Current participation in ITI therapy. * The use of emicizumab (Hemlibra®) or any non-factor bleed management treatment within 6 months prior to screening * Prior gene therapy * Current or future participation in another clinical study, scheduled to occur during this study, involving an investigational product other than fitusiran or an investigational device. * AT activity \<60% at screening, as determined by central laboratory analysis. * Co-existing thrombophilic disorder. * Presence of an active Hepatitis C virus infection * Presence of acute hepatitis A or Hepatitis E virus infection. * Presence of acute or chronic hepatitis B virus infection. * Platelet count ≤100 000/μL. * Presence of acute infection at screening. * Human immunodeficiency virus (HIV) positive with a CD4 count of \<400 cells/μL. * Estimated glomerular filtration rate ≤45 mL/min/1.73 m2 (using the Schwartz formula). The above information is not intended to contain all considerations relevant to a patient's potential participation in a clinical trial.
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What it tests

  • Fitusiran
  • Clotting factor concentrates (CFC) or bypassing agents (BPA)
  • Antithrombin concentrate (ATIIIC)
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Where

41 sites
The Luskin Orthopaedic Institute for Children- Site Number : 8400013
Los Angeles, United States
Children's Hospital Los Angeles- Site Number : 8400002
Los Angeles, United States
The Center for Inherited Blood Disorders- Site Number : 8400009
Orange, United States
UCLA Medical Center - Harbor- Site Number : 8400011
Torrance, United States
University of Miami Hospital- Site Number : 8400005
Miami, United States
Tulane University School of Medicine- Site Number : 8400026
New Orleans, United States
University of Michigan Health System - Ann Arbor- Site Number : 8400003
Ann Arbor, United States
Cure 4 The Kids Foundation- Site Number : 8400001
Las Vegas, United States

…and 33 more on ClinicalTrials.gov.

🤝 Taking part is your choice, and you can leave at any time. Only the trial team can confirm you are eligible — always decide together with your own doctor.
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