🌐 EnglishEN

AI Cure is a research tool showing open data. Not medical advice. Discuss with your doctor. Terms

🧪

Trial Match

Clinical trials test new treatments — sometimes the newest options available for a disease. Find trials that are recruiting now, near you. Open one to see its eligibility rules as simple questions to go through with your doctor.

Know your stage or your test results (such as EGFR, HER2 or BRCA)? Match trials to your own profile - nothing you type is saved.

🎯 Match trials to me

30 recruiting trials

for Glycogen Storage Diseases

GSD VI and GSD IX Natural History NCT04454216n/a1 site📍 Durham Duke University · Tests: No intervention 'Glycogen Storage Diseases (GSDs) in Indian Children- Establishing an Indian GSD (I-GSD) Registry' NCT06396546n/a37 sites📍 Guindy📍 Ahmedabad📍 Surat Institute of Liver and Biliary Sciences, India Danon Disease Natural History Study NCT06214507n/a16 sites📍 Phoenix📍 La Jolla📍 Aurora Rocket Pharmaceuticals Inc. · Tests: No intervention Gait Analysis Parameter and Upper Limb Evaluation in Adult Patients With Neurological or Metabolic Pathology NCT07136844NA1 site📍 Liège Centre Hospitalier Universitaire de Liege · Tests: Syde, Dynamometric measurements of muscle strength, The 6-minute walk test (6MWT), The 10-meter test (10MWT), The 4 sta… Natural History of Pompe Disease NCT03564561n/a1 site📍 Garches Assistance Publique - Hôpitaux de Paris A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD) NCT07282847Phase 1, Phase 29 sites📍 Phoenix📍 Irvine📍 Palo Alto AskBio Inc · Tests: AB-1009 (GAA Gene) Glycogen Storage Disease Type Ia (GSDIa) Disease Monitoring Program NCT06636383n/a19 sites📍 Orange📍 Denver📍 Hartford Ultragenyx Pharmaceutical Inc · Tests: No Intervention French Observatory for Patients with Type 3 Glycogenosis NCT06616545n/a3 sites📍 Clamart📍 Le Kremlin-Bicêtre📍 Paris Institut de Myologie, France Precision Diagnosis and Risk Stratification of Rare Cardiomyopathies Based on Novel Cardiac Magnetic Resonance Techniques NCT07336394n/a1 site📍 Beijing Chinese Academy of Medical Sciences, Fuwai Hospital A Phase 1/2, Dose-Exploration Study to Evaluate the Safety and Efficacy of BEAM-301 in Patients With Glycogen Storage Disease Type Ia (GSDIa) NCT06735755Phase 1, Phase 23 sites📍 Orange📍 Farmington📍 Houston Beam Therapeutics Inc. · Tests: BEAM-301: Single dose of BEAM-301 administered by IV Non-invasive Assessment of Liver Fibrosis in a French Cohort of Pediatric Patients With Type III Glycogen Storage Disease: Current State and Perspectives NCT07303140n/a1 site📍 Strasbourg University Hospital, Strasbourg, France Accuracy of Lactate Meter in GSDIa NCT06843330n/a1 site📍 Hartford Connecticut Children's Medical Center · Tests: blood glucose meter; blood lactate meter ATR 1072 in Participants With PRKAG2 Syndrome NCT07738107Phase 1, Phase 21 site📍 Kansas City Atrium Therapeutics · Tests: ATR 1072 Characterization of Patients With Cardiomyopathy to Identify Critical Patients Candidates for Cardiac Transplantation NCT06813443n/a3 sites📍 Bologna📍 Roma📍 Florence IRCCS Azienda Ospedaliero-Universitaria di Bologna Transcriptomic Analysis to Put an End to Misdiagnosis in Patients With Rare Muscle Diseases NCT06833489NA1 site📍 Marseille Assistance Publique Hopitaux De Marseille · Tests: ARN extraction from muscle biopsies Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD) NCT07123155Phase 228 sites📍 Irvine📍 Gainesville📍 Atlanta Shionogi · Tests: S-606001, Placebo A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of DNL952 in Adult Participants With Late-Onset Pompe Disease NCT07354724Phase 14 sites📍 Irvine📍 St Louis📍 Durham Denali Therapeutics Inc. · Tests: DNL952 Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford NCT01793168n/a2 sites📍 Sioux Falls📍 Sydney Sanford Health Rare Glycogen Storage Diseases Natural History Study NCT06795152n/a1 site📍 Durham Duke University · Tests: No intervention A Long-term Study for the Outcome of Pompe Disease NCT02399748n/a1 site📍 Taipei National Taiwan University Hospital A Clinical Trial Evaluating the Safety and Efficacy of a New Light Combination Therapy Addressing Intermediate AMD NCT06557369NA1 site📍 Bergamo Oculox Technologies SA · Tests: reSEES Brain Metabolism Observed at 3 Tesla or 7 Tesla in Health and Metabolic Disease NCT05085704n/a2 sites📍 New York📍 Dallas Weill Medical College of Cornell University · Tests: Magnetic resonance imaging Pompe Pregnancy Sub-Registry NCT00567073n/a35 sites📍 Phoenix📍 Jacksonville📍 Atlanta Genzyme, a Sanofi Company Use of Continuous Glucose Monitoring to Evaluate Postprandial Response to Raw Cornstarch Supplementation in Adult Glycogen Storage Disease Type I NCT07645898n/a1 site📍 Naples Federico II University Pompe Disease RWE Long-term Monitoring Program NCT07834320n/a1 site📍 Taipei National Taiwan University Hospital GBE Deficiency (GSD IV and APBD) Natural History Study NCT02683512n/a1 site📍 Durham Duke University · Tests: No intervention Pompe Disease Registry Protocol NCT00231400n/a272 sites📍 Birmingham📍 Phoenix📍 Phoenix Genzyme, a Sanofi Company Cognitive and Neurological Pathologies in Pompe Disease NCT04639336n/a1 site📍 Durham Duke University Determination of CRIM Status and Longitudinal Follow-up of Individuals With Pompe Disease NCT01665326n/a1 site📍 Durham Duke University · Tests: Observational Dietary Treatment Strategies and Metabolic Control in Glycogen Storage Disease Type I NCT06852612NA2 sites📍 Bern📍 Zurich Insel Gruppe AG, University Hospital Bern · Tests: Fructose, Fructose and galactose
🛡️

AI Cure shows public evidence (Open Targets, ClinicalTrials.gov, PubMed, openFDA, DepMap, AlphaFold) with its source, and AI summaries that cite it — not medical advice and not a cure. Treatment decisions belong with your doctor. Research ideas are shared only with approved researchers and labs, who can test them. In an emergency call your local emergency number (112 in India and Europe, 911 in the US). AI Cure Terms of Use · Privacy