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Clinical trials test new treatments โ€” sometimes the newest options available for a disease. Find trials that are recruiting now, near you. Open one to see its eligibility rules as simple questions to go through with your doctor.

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25 recruiting trials

for Hereditary Amyloidosis, Transthyretin-Related

Cardiac Magnetic Resonance and Echocardiography Study With Acoramidis NCT07695701Phase 41 site๐Ÿ“ St Louis Eidos Therapeutics, a BridgeBio company ยท Tests: Acoramidis (AG10) oral tablet A Study to Learn About the Use of Acoramidis in Patients With a Heart Condition Called Transthyretin Amyloid Cardiomyopathy (ATTR-CM) in a Real-world Setting NCT07235462n/a17 sites๐Ÿ“ Multiple Locations๐Ÿ“ Multiple Locations๐Ÿ“ Multiple Locations Bayer ยท Tests: Acoramidis (356 mg film-coated tablets) Characterizing Iodine-124 Evuzumitide (AT-01) in Systemic Amyloidosis NCT05758493Phase 21 site๐Ÿ“ Portland Oregon Health and Science University ยท Tests: 124I-Evuzamitide To Evaluate the Efficacy and Safety of Tafamidis Meglumine Soft Capsules in the Treatment of Adult Patients With Transthyretin Amyloid Polyneuropathy NCT06940336Phase 41 site๐Ÿ“ Jinan Qilu Pharmaceutical Co., Ltd. ยท Tests: Tafamidis Meglumine Soft Capsules Pan-Amyloid PET/CT in Various Amyloid-Related Disease NCT07130565n/a3 sites๐Ÿ“ Hefei๐Ÿ“ Qingdao๐Ÿ“ Tianjin Tianjin Medical University ยท Tests: 18F-92/AV45/TPZA/FT8, 11CPIB ConTTRibute: A Global Observational Study of Patients With Transthyretin (TTR)-Mediated Amyloidosis (ATTR Amyloidosis) NCT04561518n/a40 sites๐Ÿ“ La Jolla๐Ÿ“ Los Angeles๐Ÿ“ Jacksonville Alnylam Pharmaceuticals An Interventional Pilot Study to Investigate the Feasibility and Acceptance of a Structured Psychological Support Program for Patients, Caregivers, and Presymptomatic Carriers in Hereditary Transthyretin Amyloidosis With Cardiomyopathy NCT06907186NA1 site๐Ÿ“ Pavia Fondazione IRCCS Policlinico San Matteo di Pavia ยท Tests: Psychological Support Non-interventional Study of Patients With Transthyretin (ATTR) Amyloidosis NCT06465810n/a89 sites๐Ÿ“ La Jolla๐Ÿ“ Los Angeles๐Ÿ“ San Francisco AstraZeneca ยท Tests: Treatment of transthyretin (ATTR) amyloidosis in observational study setting Longitudinal Quantitative Neuromuscular MRI in Neuropathic Patients NCT06845644NA1 site๐Ÿ“ Marseille Assistance Publique Hopitaux De Marseille ยท Tests: Quantitative neuromuscular MRI, Neuromuscular ultrasound Long-term Safety of Eplontersen Treated aTTR Patients and in Liver Transplant and Severely Hepatic Impaired Subpopulations NCT07654855n/a6 sites๐Ÿ“ Los Angeles๐Ÿ“ Vancouver๐Ÿ“ Beijing AstraZeneca ยท Tests: None ( observational study ) A Phase 3 Study of NTLA-2001 in ATTRv-PN NCT06672237Phase 314 sites๐Ÿ“ Buenos Aires๐Ÿ“ Buenos Aires๐Ÿ“ San Juan Bautista Intellia Therapeutics ยท Tests: nexiguran ziclumeran, Normal Saline as Placebo Subclinical Transthyretin Cardiac Amyloidosis in V122I TTR Carriers NCT05489549n/a3 sites๐Ÿ“ New York๐Ÿ“ Cleveland๐Ÿ“ Dallas University of Texas Southwestern Medical Center Phenotypic Manifestations of Hereditary ATTR Amyloidosis NCT07124377n/a2 sites๐Ÿ“ Charata๐Ÿ“ Charata Hospital 9 de Julio de Las Breรฑas ยท Tests: A complete physical examination of all body systems, including height and body weight, Neurological examination includeโ€ฆ Cardiovascular Multimodality Imaging Study NCT06610019n/a1 site๐Ÿ“ The Bronx Montefiore Medical Center Comprehensive Program for Hereditary Transthyretin Amyloidosis NCT07213297n/a1 site๐Ÿ“ Canuelas Hospital de Alta Complejidad en Red ยท Tests: clinical assessments and complementary examinations TRITON-PN: A Study to Evaluate the Efficacy and Safety of Nucresiran in Patients With Hereditary Transthyretin Amyloidosis With Polyneuropathy NCT07223203Phase 361 sites๐Ÿ“ Aurora๐Ÿ“ Chicago๐Ÿ“ Baltimore Alnylam Pharmaceuticals ยท Tests: Nucresiran, Vutrisiran The Eplontersen Pregnancy and Lactation Outcomes Study NCT07205666n/a1 site๐Ÿ“ Frankfurt AstraZeneca MAGNITUDE: A Phase 3 Study of NTLA-2001 in Participants With Transthyretin Amyloidosis With Cardiomyopathy (ATTR-CM) NCT06128629Phase 3132 sites๐Ÿ“ Tucson๐Ÿ“ Los Angeles๐Ÿ“ Los Angeles Intellia Therapeutics ยท Tests: NTLA-2001, Placebo Acoramidis Transthyretin Amyloidosis Prevention Trial in the Young (ACT-EARLY) Study in Asymptomatic Carriers of a Pathogenic TTR Variant NCT06563895Phase 3104 sites๐Ÿ“ La Jolla๐Ÿ“ Los Angeles๐Ÿ“ San Francisco Eidos Therapeutics, a BridgeBio company ยท Tests: Acoramidis, Placebo oral tablet Exercise in Hereditary ATTR (ATTRv) Amyloidosis NCT07033715NA1 site๐Ÿ“ Maia University of Maia ยท Tests: Exercise Prevalence and Prediction of ATTR in Ambulatory Patients With HFpEF NCT05577819NA1 site๐Ÿ“ Boston Massachusetts General Hospital ยท Tests: 99mTc-pyrophosphate Scintigraphy Determining the Association of TTR Stabilizing Therapy With Circulating TTR Amyloid Aggregates Over Time in Patients With ATTR-CM: Longitudinal Biomarker Study NCT07196839n/a1 site๐Ÿ“ Dallas University of Texas Southwestern Medical Center Phenotyping and Characterization of wtATTR-CM (TRACE 1) NCT06291805n/a1 site๐Ÿ“ Aarhus Steen Hvitfeldt Poulsen Concordance for Transthyretin Amyloidosis Between Synovial Biopsy and Anterior Carpal Ligament Biopsy NCT07644325NA1 site๐Ÿ“ Montpellier Clinique Saint Jean, France ยท Tests: Annular ligament biopsy Liver and Coagulation Disorders in Cardiac Transthyretin Amyloidosis NCT07766135n/a1 site๐Ÿ“ Messina University of Messina
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