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Trial Match

Clinical trials test new treatments — sometimes the newest options available for a disease. Find trials that are recruiting now, near you. Open one to see its eligibility rules as simple questions to go through with your doctor.

Know your stage or your test results (such as EGFR, HER2 or BRCA)? Match trials to your own profile - nothing you type is saved.

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17 recruiting trials

for Primary Mitochondrial Diseases

Prospective Natural History Study of POLG Disease NCT07775872n/a21 sites📍 San Diego📍 Aurora📍 New York The POLG Foundation Open Label Extension to Assess Long Term Safety and Efficacy of KL1333 in Patients With Primary Mitochondrial Disease NCT07514338Phase 223 sites📍 Akron📍 Brussels📍 Brussels Pharming Technologies B.V. · Tests: Napazimone Systemic Biomarkers of Brain Injury From Hyperammonemia NCT04602325n/a1 site📍 Washington D.C. Children's National Research Institute Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford NCT01793168n/a2 sites📍 Sioux Falls📍 Sydney Sanford Health KHENERFIN Study: A Trial to Evaluate the Efficacy and Safety of Sonlicromanol in Primary Mitochondrial Diseases NCT06451757Phase 310 sites📍 Boston📍 Cleveland📍 Houston Khondrion BV · Tests: Sonlicromanol, Placebo Triheptanoin for Children With Primary-Specific Pyruvate Dehydrogenase Complex (PDC) Deficiency NCT06340685Phase 11 site📍 Pittsburgh Jirair Krikor Bedoyan · Tests: Triheptanoin Doxecitin and Doxribthymine in Adult Subjects With Thymidine Kinase 2 (TK2) Deficiency NCT06754098Phase 21 site📍 Madrid Cristina Domínguez González · Tests: Doxecitine and Doxribtimine Early Diagnosis of Primary Biliary Cholangitis (PBC) in Patients With Positive Anti-Mitochondrial Antibodies (AMA) and Normal Alkaline Phosphatase (ALP) NCT07205874n/a1 site📍 Madrid Hospital Universitario La Paz Collection of Blood and Skin Samples From Patients With Primary Mitochondrial Diseases and Healthy Volunteers NCT06474104n/a1 site📍 Ramat Gan Minovia Therapeutics Ltd. Efficacy of KL1333 in Adult Patients With Primary Mitochondrial Disease NCT05650229Phase 255 sites📍 Orange📍 San Diego📍 San Francisco Pharming Technologies B.V. · Tests: KL1333, Placebo Applying pGz in Mitochondrial Disease NCT05569122Phase 11 site📍 Philadelphia Children's Hospital of Philadelphia · Tests: Cardiopulmonary Exercise Testing, pGz Bed, Gentle Jogger, Exercise Pedal, Lumason® contrast agent Neurometabolic Profile of Individuals With Primary Mitochondrial Disease NCT06890520n/a1 site📍 Philadelphia Children's Hospital of Philadelphia Effects of Whole-body Electrical Muscle Stimulation Exercise on Adults With Neuromuscular Disease NCT07478172NA1 site📍 Columbia University of Missouri-Columbia · Tests: Whole-body Electrical Muscle Stimulation Exercise Polycystic Ovary Syndrome, Mitochondrial Dysfunction, Obesity, Insulin Resistance Infertility (POMODORI) Cohort NCT06167135n/a1 site📍 Budapest Semmelweis University Natural History Study of Mitochondrial Myopathy NCT05250375n/a1 site📍 Philadelphia Children's Hospital of Philadelphia National Registry of Rare Kidney Diseases NCT06065852n/a1 site📍 Bristol UK Kidney Association Idebenone for the Preventive Treatment of Migraine NCT04151472Phase 31 site📍 Hangzhou Second Affiliated Hospital, Zhejiang University, School of … · Tests: Placebo, 90mg Idebenone, 270mg Idebenone
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