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Trial Match

Clinical trials test new treatments — sometimes the newest options available for a disease. Find trials that are recruiting now, near you. Open one to see its eligibility rules as simple questions to go through with your doctor.

Know your stage or your test results (such as EGFR, HER2 or BRCA)? Match trials to your own profile - nothing you type is saved.

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30 recruiting trials

for Rare Diseases

An International Study on Pediatric Patients With Rare Tumors. NCT07072143n/a1 site📍 Padova Azienda Ospedaliera di Padova A Study of Zipalertinib in Patients With Advanced Non-Small Cell Lung Cancer With Epidermal Growth Factor Receptor (EGFR) Exon 20 Insertions or Other Uncommon Mutation. NCT05967689Phase 280 sites📍 Birmingham📍 Duarte📍 Boston Taiho Oncology, Inc. · Tests: TAS6417, CYP Cocktail, Transporter Cocktail CS-121 APOC3 Base Editing in FCS NCT07176923EARLY Phase 11 site📍 Hefei CorrectSequence Therapeutics Co., Ltd · Tests: CS-121 Natural History of Uncommon Dyslipidemias, Rare Lipid Disorders and Unusual Atherosclerotic Conditions NCT06676046n/a1 site📍 Bethesda National Heart, Lung, and Blood Institute (NHLBI) Assessing the Impact of Intensification of Lipid Lowering Therapy With Guidelines-based Evinacumab Administration on Coronary Plaque Volumes Measured by Coronary Computed Tomography Angiography (CCTA) in Patients With Homozygous Familial Hypercholesterolemia (HoFH) NCT07447648n/a13 sites📍 Paris📍 Caserta📍 Catania Fondazione SISA (Societa Italiana per lo Studio della Arter… Using a Speech-Generating Device to Support Communication in Rare Genetic Conditions NCT07039084NA1 site📍 Melbourne Murdoch Childrens Research Institute · Tests: Speech-generating device, Control Exome and Genome Sequencing of DNA Samples, as Required by Specific Research Projects and the Diagnostic Needs of the Gaslini Institute, to Be Performed Within the Framework of the "Joint Genomic Lab" Established Between IGG and IIT NCT07877688n/a1 site📍 Genova Istituto Giannina Gaslini Multi-Omics Genetic Investigation Strategies to Enhance the Diagnostic Workflow for Rare Diseases NCT07884227n/a1 site📍 Genova Istituto Giannina Gaslini Performance Indicators and Impact on the Care Pathway of Sequencing on the SeqOIA and AURAGEN (Seqogen) Platforms for Oncology Patients NCT07147465n/a3 sites📍 Lyon📍 Paris📍 Paris Assistance Publique - Hôpitaux de Paris Rare AutoImmune SElf-management Programme Development NCT06642870n/a1 site📍 Bristol University of the West of England · Tests: Non-interventional study Assessing Pulmonary Changes in HSCT NCT07823036Phase 1, Phase 21 site📍 Cincinnati Children's Hospital Medical Center, Cincinnati · Tests: Hyperpolarized 129 Xenon Education & Care in RARE: Efficacy of Targeted Psychoeducational Intervention Among Pediatric Rare Disease Patients NCT06729554NA7 sites📍 Graz📍 Innsbruck📍 Linz Medical University of Vienna · Tests: Education & Care in RARE International Rare And Severe Psoriasis Expert Network NCT04359394n/a8 sites📍 München📍 Rome📍 Porto University Hospital, Basel, Switzerland · Tests: biological sampling, Phenotypic description, Photography Observational Study for Patients With Hemoglobinopathies and Rare Inherited Anemia and Covid 19 NCT04746066n/a2 sites📍 Genova📍 Genova Società Italiana Talassemie ed Emoglobinopatie Transition of Care in Pediatric Rare Endocrine Disorders NCT07786142NA11 sites📍 Daegu📍 Daegu📍 Daejeon Seoul National University Hospital · Tests: Structured Transition-of-Care Program Elafibranor Pregnancy Surveillance Program: A Study to Evaluate the Safety of Elafibranor During Pregnancy NCT07556913n/a1 site📍 Wilmington Ipsen · Tests: Elafibranor B-dependant Rare AutoImmune diseaSES - Cohort of Patients With Suspected Diagnosis of Primitive Sjögren Syndrome NCT04931160NA1 site📍 Brest University Hospital, Brest · Tests: Blood, fluid, sells and urine samples Characterization and Contribution of Genome-wide DNA Methylation (DNA Methylation Episignatures) in Rare Diseases With Prenatal Onset NCT06475651n/a1 site📍 Paris Assistance Publique - Hôpitaux de Paris · Tests: Methylation analysis Study to Evaluate Sutetinib Maleate Capsule in Locally Advanced or Metastatic Non-small Cell Lung Cancer NCT05168566Phase 231 sites📍 Glendale📍 Washington D.C.📍 Athens Teligene US · Tests: Sutetinib Maleate Capsule Rare Disease Registry Database for Movement Disorders in Southern Anhui Province NCT07838883n/a1 site📍 Wuhu First Affiliated Hospital of Wannan Medical College Orodental Manifestations of Rare Diseases NCT02397824n/a1 site📍 Strasbourg University Hospital, Strasbourg, France · Tests: Salivary and blood samples Precision Diagnosis and Therapy for Rare Diseases by Interpreting Non-coding Genomes NCT06775561n/a1 site📍 Bologna IRCCS Azienda Ospedaliero-Universitaria di Bologna · Tests: PARADIGM study aims to streamline the process from genomic characterization of RGD patients with ED/NMD to identificati… Dabrafenib and/or Trametinib Rollover Study NCT03340506Phase 438 sites📍 Scottsdale📍 Bethesda📍 Columbus Novartis Pharmaceuticals · Tests: dabrafenib, trametinib Eurbio-Alport (RaDiCo Cohort) (RaDiCo Eurbio-Alport) NCT05927467n/a1 site📍 Paris Institut National de la Santé Et de la Recherche Médicale, … Genomic Uniformed-Screening Against Rare Disease In All Newborns NCT05990179NA1 site📍 New York Columbia University · Tests: Genome sequencing-based newborn screening A First-in-Human Clinical Trial to Evaluate the Safety, Tolerability, and Efficacy of a Novel CRISPR RNA-editing Therapy in Patients with Mecp2 Duplication Syndrome, a Rare Orphan Disease (HERO) NCT06615206NA1 site📍 Beijing HuidaGene Therapeutics Co., Ltd. · Tests: HG204 Genetic Aortic Diseases and Cardiovascular Complications. An Observational Survey of Risk Factors. NCT07391293n/a1 site📍 Milan IRCCS Policlinico S. Donato · Tests: Journey to diagnosis, Quality of life, functional health and well-being, Awareness and self-esteem, acceptance of the c… Solving Riddles Through Sequencing NCT05046444n/a1 site📍 Munich Munich Leukemia Laboratory · Tests: Next Generation Sequencing Nephrotic Syndrome Study Network NCT01209000n/a44 sites📍 Los Angeles📍 Palo Alto📍 San Francisco University of Michigan · Tests: Kidney Biopsy ScATtEred Rare Disease Biobanks: a Model of Sample/Data Collection With susTainablE and Shared Criteria NCT06782230n/a1 site📍 San Donato Milanese IRCCS Policlinico S. Donato
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