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Clinical trials test new treatments โ€” sometimes the newest options available for a disease. Find trials that are recruiting now, near you. Open one to see its eligibility rules as simple questions to go through with your doctor.

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30 recruiting trials

for Amyloidosis, Hereditary

Prognosis of Cerebral Small Vessel Disease NCT05734378n/a1 site๐Ÿ“ Bern Insel Gruppe AG, University Hospital Bern Cardiac Amyloidosis Registry of University Hospital Leipzig NCT06129656n/a1 site๐Ÿ“ Leipzig University of Leipzig ยท Tests: Routine diagnostics, Routine treatment Patisiran-Lipid Nanoparticle (LNP) Pregnancy Surveillance Program NCT05040373n/a7 sites๐Ÿ“ Iowa City๐Ÿ“ Nantes๐Ÿ“ Mรผnster Alnylam Pharmaceuticals Cardiac Magnetic Resonance and Echocardiography Study With Acoramidis NCT07695701Phase 41 site๐Ÿ“ St Louis Eidos Therapeutics, a BridgeBio company ยท Tests: Acoramidis (AG10) oral tablet Multimodal Analysis of Endomyocardial Biopsies NCT07359690n/a1 site๐Ÿ“ Essen University Hospital, Essen Essen Amyloidosis Registry NCT06887283n/a1 site๐Ÿ“ Essen University Hospital, Essen Repeat PET/CT Imaging in People With CAPS and Anakinra-Induced Amyloidosis Using an Amyloid-Reactive Peptide to Measure Changes in Organ-Specific Amyloid Load NCT06974877Phase 11 site๐Ÿ“ Bethesda National Institute of Allergy and Infectious Diseases (NIAIโ€ฆ ยท Tests: 124I AT-01 Amylo-Shiatsu-Acute-Chronic: Effects of Shiatsu on Symptoms and Quality of Life of Amyloidosis Patients NCT06197165NA1 site๐Ÿ“ Crรฉteil Assistance Publique - Hรดpitaux de Paris ยท Tests: Targeted Shiatsu A Study to Learn About the Use of Acoramidis in Patients With a Heart Condition Called Transthyretin Amyloid Cardiomyopathy (ATTR-CM) in a Real-world Setting NCT07235462n/a17 sites๐Ÿ“ Multiple Locations๐Ÿ“ Multiple Locations๐Ÿ“ Multiple Locations Bayer ยท Tests: Acoramidis (356 mg film-coated tablets) SKIN Disease Profiling by an Exploratory, pRospective, Biomarker Study in dermatoloGY Practice (SKINERGY) NCT07021495n/a8 sites๐Ÿ“ Nijmegen๐Ÿ“ Maastricht๐Ÿ“ Amsterdam Leiden University Medical Center Precision Diagnosis and Risk Stratification of Rare Cardiomyopathies Based on Novel Cardiac Magnetic Resonance Techniques NCT07336394n/a1 site๐Ÿ“ Beijing Chinese Academy of Medical Sciences, Fuwai Hospital Genistein in trAnSthyretin recePtor Amyloid caRdiomyopathy NCT06634108Phase 1, Phase 21 site๐Ÿ“ London London Health Sciences Centre Research Institute OR Lawson โ€ฆ ยท Tests: Genistein Characterizing Iodine-124 Evuzumitide (AT-01) in Systemic Amyloidosis NCT05758493Phase 21 site๐Ÿ“ Portland Oregon Health and Science University ยท Tests: 124I-Evuzamitide To Evaluate the Efficacy and Safety of Tafamidis Meglumine Soft Capsules in the Treatment of Adult Patients With Transthyretin Amyloid Polyneuropathy NCT06940336Phase 41 site๐Ÿ“ Jinan Qilu Pharmaceutical Co., Ltd. ยท Tests: Tafamidis Meglumine Soft Capsules Pan-Amyloid PET/CT in Various Amyloid-Related Disease NCT07130565n/a3 sites๐Ÿ“ Hefei๐Ÿ“ Qingdao๐Ÿ“ Tianjin Tianjin Medical University ยท Tests: 18F-92/AV45/TPZA/FT8, 11CPIB DZHK TORCH-Plus is a Registry for Patients With Cardiomyopathies and Serves as Source for Cardiovascular Research Studies NCT04265040n/a1 site๐Ÿ“ Heidelberg University Hospital Heidelberg Characterization of Patients With Cardiomyopathy to Identify Critical Patients Candidates for Cardiac Transplantation NCT06813443n/a3 sites๐Ÿ“ Bologna๐Ÿ“ Roma๐Ÿ“ Florence IRCCS Azienda Ospedaliero-Universitaria di Bologna Effect of the Mediterranean Diet in Patients Affected by CADASIL and Cerebral Amyloid Angiopathy. NCT06933212n/a1 site๐Ÿ“ Milan Fondazione I.R.C.C.S. Istituto Neurologico Carlo Besta ยท Tests: Mediterranean Diet with Extra Virgin Olive Oil, Mediterranean Diet with Walnuts, Low-Fat Control Diet A Cohort Study of Plasma Cell Disorders (PCDs) in PKUFH NCT05283993n/a1 site๐Ÿ“ Beijing Peking University First Hospital ยท Tests: No intervention ConTTRibute: A Global Observational Study of Patients With Transthyretin (TTR)-Mediated Amyloidosis (ATTR Amyloidosis) NCT04561518n/a40 sites๐Ÿ“ La Jolla๐Ÿ“ Los Angeles๐Ÿ“ Jacksonville Alnylam Pharmaceuticals An Interventional Pilot Study to Investigate the Feasibility and Acceptance of a Structured Psychological Support Program for Patients, Caregivers, and Presymptomatic Carriers in Hereditary Transthyretin Amyloidosis With Cardiomyopathy NCT06907186NA1 site๐Ÿ“ Pavia Fondazione IRCCS Policlinico San Matteo di Pavia ยท Tests: Psychological Support Non-interventional Study of Patients With Transthyretin (ATTR) Amyloidosis NCT06465810n/a89 sites๐Ÿ“ La Jolla๐Ÿ“ Los Angeles๐Ÿ“ San Francisco AstraZeneca ยท Tests: Treatment of transthyretin (ATTR) amyloidosis in observational study setting Cardiac Amyloid Deposits and Heart Dysfunction in Alzheimer's Disease NCT07154394n/a1 site๐Ÿ“ Essen University Hospital, Essen Hungarian National Systemic Amyloidosis Registry NCT07689331n/a12 sites๐Ÿ“ Balatonfรผred๐Ÿ“ Budapest๐Ÿ“ Budapest Semmelweis University Longitudinal Quantitative Neuromuscular MRI in Neuropathic Patients NCT06845644NA1 site๐Ÿ“ Marseille Assistance Publique Hopitaux De Marseille ยท Tests: Quantitative neuromuscular MRI, Neuromuscular ultrasound A Study to Assess the Effects of ACI-24.060 in Alzheimer's Disease and in Down Syndrome (ABATE Study) NCT05462106Phase 1, Phase 226 sites๐Ÿ“ Phoenix๐Ÿ“ Lady Lake๐Ÿ“ Orlando AC Immune SA ยท Tests: Placebo (Study Part 1a), ACI-24.060 at Dose A in Study Part 1a, ACI-24.060 at Dose B in Study Part 1a, ACI-24.060 at Doโ€ฆ Long-term Safety of Eplontersen Treated aTTR Patients and in Liver Transplant and Severely Hepatic Impaired Subpopulations NCT07654855n/a6 sites๐Ÿ“ Los Angeles๐Ÿ“ Vancouver๐Ÿ“ Beijing AstraZeneca ยท Tests: None ( observational study ) A Phase 3 Study of NTLA-2001 in ATTRv-PN NCT06672237Phase 314 sites๐Ÿ“ Buenos Aires๐Ÿ“ Buenos Aires๐Ÿ“ San Juan Bautista Intellia Therapeutics ยท Tests: nexiguran ziclumeran, Normal Saline as Placebo ATTR Cardiac Amyloidosis in a Selected Population NCT06458374n/a1 site๐Ÿ“ ร…lesund Helse Mรธre og Romsdal HF Ultrasound Therapy In Cardiac Amyloidosis NCT04667494Phase 41 site๐Ÿ“ Boston Brigham and Women's Hospital ยท Tests: Sonotherapy
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